I CAN
TREAT MY
FA PROGRESSION

SKYCLARYS is used for the treatment of Friedreich ataxia (FA) in adults and children aged 16 years and older

Talk to your doctor to see if SKYCLARYS is right for you. It is not known if SKYCLARYS is safe and effective for use in children younger than 16 years of age

SKYCLARYS is the first and only FDA-approved prescription medicine to treat FA for patients 16 years and older

Understanding FA

What is FA?

FA is a rare, genetic, progressive disease that damages the nervous system, causing you to lose control of your muscles over time.

What causes FA?

FA happens when a specific gene, called the frataxin gene (or FXN), does not function properly and cannot help nerve cells work the way they should. Ultimately, this leads to irreversible cell death.

How is FA diagnosed?

FA can be confirmed with a genetic test. It is important that the test includes a Friedreich Ataxia Repeat Expansion Analysis. Your doctor can provide additional information about the specific test needed.

What happens as FA progresses?

As you get older, FA continues to damage nerve cells, which leads to greater difficulty with things like:

Standing

Walking

Talking

Fine motor skills

How can FA progression be measured?

The severity of FA can be measured in different ways—one way is the modified Friedreich Ataxia Rating Scale (mFARS).

Most people with FA will need to use a wheelchair around 10 to 15 years after the onset of symptoms. In addition to difficulty moving and talking, FA may cause a serious heart condition called cardiomyopathy. With cardiomyopathy, the muscles in the heart become damaged, making it harder for the heart to pump blood.